From Gaza's Shadow to Italy's Embrace: A Toddler's Miraculous Recovery from Rare Disease and Malnutrition

Kerala Teen's Miraculous Escape: Surviving the World's First Dual Amoebic and Fungal Brain Infection

The Unyielding Quest: NJ Parents Defy Big Pharma to Forge Cures for Their Children

A Silent Predator's Toll: Missouri Patient Succumbs to Brain-Eating Amoeba

Unraveling Bloom Syndrome: A Comprehensive Guide to a Rare Genetic Condition

Rare Plague Case Confirmed: California Resident Recovers Amidst Public Health Scrutiny

A New Hope for Danon Disease: FDA Lifts Clinical Hold on Rocket Pharma's Groundbreaking Gene Therapy

Unlocking Hope: The Global Race for a Cure in Focal Segmental Glomerulosclerosis

A New Dawn for Rare Disease Treatment: FDA Approves Groundbreaking Gene Therapy for DEB