Regeneron's Evkeeza Achieves Landmark FDA Approval, Extending Life-Saving Treatment to Youngest HoFH Patients

A New Dawn: Groundbreaking Treatment Offers Unprecedented Hope Against Huntington's Disease

Historic Breakthrough: First Drug Successfully Lowers Huntington's Disease Protein in Humans

A New Dawn: Scientists Achieve Landmark Breakthrough in Treating Huntington's Disease

Gene Therapy Delivers Staggering 75% Slowdown in Huntington's Progression, Offers New Hope

University of Alberta to Honour Biology Grad for Groundbreaking Cystic Fibrosis Breakthrough

Understanding Alpha Thalassemia: A Comprehensive Guide to Types, Symptoms, and Diagnosis

Life-Changing Breakthrough: Cystic Fibrosis Drug Earns Developers Prestigious "American Nobel" for Decades of Extended Life

A New Dawn for Rare Skin Diseases: Gene Therapy Revolutionizes Epidermolysis Bullosa Treatment

The Unyielding Quest: NJ Parents Defy Big Pharma to Forge Cures for Their Children

Revolutionizing Early Diagnosis: A New Dawn for Alpha-1 Patients